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Is there any permanent cure for Duchenne muscular dystrophy?

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Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR gene-editing technology inside cells, and have demonstrated in mice that it can repair the faulty gene mutation that causes the severe muscle-wasting disease Duchenne muscular dystrophy. read more

NO there is no permanent cure for DMD but physiotherapy surly does help in maintaining the quality of life. A drug called Eteplirsen [Exondys 51] was recently approved by FDA in USA but that is too costly for $300000/years and has been found to be effective only in 13% of cases. read more

Duchenne Muscular Dystrophy (DMD) Research Scientists around the globe are conducting intense research to understand what causes muscle dysfunction in Duchenne muscular dystrophy (DMD) and to apply that understanding to the development of effective treatments. read more

To learn more about Duchenne muscular dystrophy or find a support group in your area, visit: Cure Duchenne, the Muscular Dystrophy Association, or the Parent Project Muscular Dystrophy. read more

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