Is there any treatment for Duchenne muscular dystrophy?

There is no cure for any form of muscular dystrophy, but medications and therapy can slow the course of the disease. Human trials of gene therapy with the dystrophin gene are on the near horizon. For instance, scientists are researching ways to insert a working dystrophin gene into the muscles of boys with Duchenne and Becker muscular dystrophies. read more

Duchenne muscular dystrophy (DMD) is associated with the most severe clinical symptoms as compared to Becker muscular dystrophy (BMD) which has milder symptoms. Calling it DMD the therapy is aimed at initial treatment with Glucocorticoids as the mainstay, and are offered for patients four years of age and older whose motor skills have plateaued or are declining. read more

For more, see FDA Approves Emflaza for Treatment of Duchenne Muscular Dystrophy. MDA has invested heavily in researchers who are working on developing new anti-inflammatory therapies that have fewer or less severe side effects than the corticosteroids currently in use. read more