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What are the latest successes in gene therapy?

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Since then, researchers have begun trials with new, safer viral vectors that are much less likely to cause cancer. Adenosine deaminase (ADA) deficiency is another inherited immune disorder that has been successfully treated with gene therapy. read more

Gene Therapy Successes Researchers have been working for decades to bring gene therapy to the clinic, yet very few patients have received any effective gene-therapy treatments. But that doesn't mean gene therapy is an impossible dream. read more

Strimvelis™, one of the most recently approved gene therapy, received a market authorization from the European Commission in May 2016. In addition, over 500 gene therapy candidates are in different stages of clinical development; for these, approximately 1,700 clinical studies are currently being conducted in various regions across the globe. read more

Experimental gene therapy trials have improved the vision of four people who suffer from hereditary blindness. The preliminary results of two independent studies suggest that “repair” genes delivered to the eye might one day cure Leber congenital amaurosis (LCA), a rare disease that strikes about 1 in 80,000 people in the UK, and 2,000 Americans in total. read more

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Gene therapy pioneered at St. Jude shows early success ...
Source: multivu.com

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Gene Therapy News -- ScienceDaily
www.sciencedaily.com

Gene Therapy Successes
learn.genetics.utah.edu

Successes and setbacks of clinical gene therapy
www.gesundheitsindustrie-bw.de