On December 19, 2017, the FDA approved Voretigene Neparvovec (Luxturna, Spark Therapeutics), an innovative one-time gene therapy treatment used to improve ... read more
Click here for an overview of new gene therapy trials or search trials by indication. Among the most notable advancements in gene therapy are the following. See also Major developments in gene therapy, Gene Therapy: Medicine of the 21st Century and Individualized Drugs & Gene Therapy (video 6). read more